The first Huntington patients ever have received gene therapy!
The first two patients in uniQure’s in-human gene therapy trial for Huntington’s disease (HD) have now been treated. The dosing of the drug called AMT-130 in the trial marks a significant milestone for uniQure and for Huntington patients in need of treatment options. At this stage, safety, tolerance and efficacy of the treatment are being tested. 26…
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