Join Rare Disease Day!

29 February 2020 will be the thirteenth international Rare Disease Day. On this day, hundreds of patient organisations will hold awareness-raising activities.

29 February 2020 will be the thirteenth international Rare Disease Day. On this day, hundreds of patient organisations will hold awareness-raising activities.

29 February 2020 will be the thirteenth international Rare Disease Day. On this day, hundreds of patient organisations will hold awareness-raising activities.

Trial Finder Launched in Europe

We have launched the first HD Trial Finder in Europe! The platform makes it easier to find out more about Huntington’s disease (HD) trials and studies in Europe.

We have launched the first HD Trial Finder in Europe! The platform makes it easier to find out more about Huntington’s disease (HD) trials and studies in Europe.

We have launched the first HD Trial Finder in Europe! The platform makes it easier to find out more about Huntington’s disease (HD) trials and studies in Europe.

Exciting results from Wave Trial PRECISION-HD2!

Today, December 30, Wave announced the first preliminary results from the their study PRECISION-HD2. So far the results are very exciting and promising. 

Today, December 30, Wave announced the first preliminary results from the their study PRECISION-HD2. So far the results are very exciting and promising. 

Today, December 30, Wave announced the first preliminary results from the their study PRECISION-HD2. So far the results are very exciting and promising. 

First human gene therapy trial in Huntington’s disease

uniQure is currently developing a gene therapy treatment. In 2019, FDA gave permission to start human trials in the United States. It will be the first gene therapy trial ever in Huntington's disease.

uniQure is currently developing a gene therapy treatment. In 2019, FDA gave permission to start human trials in the United States. It will be the first gene therapy trial ever in Huntington's disease.

uniQure is currently developing a gene therapy treatment. In 2019, FDA gave permission to start human trials in the United States. It will be the first gene therapy trial ever in Huntington's disease.

previous arrowprevious arrow
next arrownext arrow
Slider

NEWS


JOIN RARE DISEASE DAY 2020!

29 February 2020 will be the thirteenth international Rare Disease Day coordinated by EURORDIS. On and around this day hundreds of patient organisations from countries ...
Read More
Left to right: Anne Lennon Bird, Svein Olaf Olsen and Astri Arnesen.

Unpacking Wave’s PRECISION-HD2 huntingtin-lowering trial announcement

Just before the new year, Wave announced that the drug in the PRECISION-HD2 trial had successfully lowered the concentration of mutant huntingtin in the spinal ...
Read More

Trial Finder Launched in Europe

This Christmas, we launched the first HD Trial Finder in Europe. HD Trial Finder is a platform developed to make it easier for you to ...
Read More


CONTACT US

Astri Arnesen
President