Prilenia Enters into a Collaboration and License Agreement with Ferrer for the Commercialization and Co-Development of Pridopidine in Europe and Other Select Markets
Prilenia and Ferrer Partner to Advance Pridopidine in Europe and Select Markets What do we know? Prilenia has entered into a significant collaboration with Ferrer to commercialize and further develop pridopidine in Europe and select markets. Pridopidine is a potent and highly selective orally administered sigma-1 receptor (S1R) agonist designed to regulate key neuroprotective mechanisms […]
Why should the HD community be involved in Health Technology Assessments?
Why should the HD community be involved in Health Technology Assessments? In our previous article about Health Technology Assessments (HTAs), we explained what HTAs are and why they matter. If you haven’t had the chance to read it, we suggest you take a look and then come back here, since there is valuable information […]
uniQure’s Gene Therapy for Huntington’s Disease Receives Special FDA Designation
uniQure’s Gene Therapy for Huntington’s Disease Receives Special FDA Designation What do we know? uniQure has announced that their experimental gene therapy, AMT-130, has received Regenerative Medicine Advanced Therapy (RMAT) designation from the U.S. Food and Drug Administration (FDA). AMT-130 is a gene therapy that aims to slow the progression of HD by targeting and […]
update on the Phase II GENERATION HD2 study Roche announces study continuation and adjusts dosing strategy for tominersen in early-stage HD patients What do we know? Roche has announced the continuation of the GENERATION HD2 Phase II clinical trial evaluating tominersen in individuals with early signs of Huntington’s disease. Following an interim analysis by an […]
Registration is now open for the 2025 EHA Conference
Registration is now open for the 2025 EHA Conference The European Huntington Association (EHA) is pleased to announce that registration is now open for its 5th Biennial Conference, which will take place in Bucharest (Romania) from 25 to 28 September 2025. Under the slogan ‘Let’s shape our future together, we are the change!’, the conference […]
Growing Up with Hd – Insights & Support Strategies with Siri Hagen Kjølaas
Growing Up with Hd: Insights & Support Strategies with Siri Hagen Kjølaas At last year’s EHDN & Enroll-HD Conference in Strasbourg, we had the privilege of interviewing Siri Hagen Kjølaas, Ph.D., to discuss her groundbreaking research on the psychosocial challenges faced by families living with Huntington’s Disease (HD). Siri, who earned her Ph.D. from the […]
SOMBIOTECH sharing very positive trial results!
SOM BIOTECH sharing very positive trial results! SOM Biotech shared on February 6th a press release where you announced very positive results from the Phase 2 trial that was finished last year. In this trial the drug named SOM3355 in 140 patients. This drug has been used for other diseases for several decades and SOM […]
Rare Disease Day 2025 Campaign
Rare Disease Day 2025 Campaign The European Huntington Association, together with the International Huntington Association, is organizing a special campaign for Rare Disease Day 2025 on February 28th! This year’s slogan is “More than you can imagine”, and we want to showcase that people in the HD community are so much more than the disease. […]
What are Health Technology Assessments and why do they matter? Understanding the path to access to therapies
What are Health Technology Assessments and why do they matter? Understanding the path to access to therapies Health technologies include medications, devices, and systems designed to address health problems, improve health outcomes, and enhance the quality of care. For Huntington’s Disease (HD), health technologies include potential therapies that, if developed, could profoundly impact patients’ lives. […]
EHA Conference 2025 Romania
EHA CONFERENCE IN ROMANIA 2025 We are excited to announce that the European Huntington Association will be organising its 5th Biennal Conference in Bucharest, Romania, from September 25th-28th, 2025. “Shaping our Future Together, We are the Change!” encapsulates the spirit of this year’s conference, uniting the HD community to exchange experiences, explore care and treatment […]