This HD clinical trial will explore the safety, tolerability, and efficacy signals in 26 total patients with early manifest HD. “We are very pleased with the progress that we continue to make in this Phase 1-2 clinical trial and that we are now administering AMT-130 at the higher dose,” said Ricardo Dolmetsch, Ph.D., president of research at uniQure.
Scientists identify precisely how pridopidine works in models of Huntington’s disease.
Pridopidine is a drug developed to treat Huntington’s disease (HD) and now scientists have a clearer understanding of how it works in the body and brain.
Improving access to care and treatment for Huntington’s Disease patients and families
Today, only a minority of people affected by HD get the support and help they need. But there are solutions to this problem – expertise and knowledge exists – we only need to provide better access to all patients.
Life with HD comes in many flavours - alice wexler
During the webinar Annette
Listen to what the well known HD family member, academic and patient advocate from the US, Alice Wechsler, has to say about what life with HD can be like.
Join our Light
it up 4 HD!
How to take action:
- Light your house with purple or blue
- Take a picture
- Upload it on social media and add #LIGHTITUP4HD
- Tag us! @TheEuroHuntington
As you all remember in March the independent Data Monitoring Committee advised Roche to halt dosing of the drug Tominersen. On April 27 Scott Schobel, Medical Director & Clinical Science Leader at Roche shared the interim analyses of the results from the Generation HD1 at the CHDI therapeutics conference.
During the Awareness month we are organizing several webinars, articles and multiple ways to include everyone into our activities. Try our Facebook Frame for the May month!